Novel CFTR modulator combinations maximise rescue of G85E and N1303K in rectal organoids
Marjolein M. Ensinck, Liesbeth De Keersmaecker, Anabela S. Ramalho, Senne Cuyx, Stephanie Van Biervliet, Lieven Dupont, Frauke Christ, Zeger Debyser, François Vermeulen, Marianne S. Carlon
ERJ Open Research Apr 2022, 8 (2) 00716-2021; DOI: 10.1183/23120541.00716-2021