Abstract
Recommended respiratory tests used as major outcomes in clinical trials for MPS treatment cannot be routinely performed in everyday practice because neurocognitive impairment and motor skill difficulties affect compliance for most MPS patients.
Footnotes
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Conflict of interest: Dr. DENAMUR has nothing to disclose.
Conflict of interest: Dr. TOUATI has nothing to disclose.
Conflict of interest: Dr. DEBELLEIX has nothing to disclose.
Conflict of interest: Dr. Damaj has nothing to disclose.
Conflict of interest: Dr. BARTH has nothing to disclose.
Conflict of interest: Dr. TARDIEU has nothing to disclose.
Conflict of interest: Dr. GORCE has nothing to disclose.
Conflict of interest: Dr. Broué has nothing to disclose.
Conflict of interest: Dr. LACOMBE reports personal fees from Sanofi - Genzyme, outside the submitted work; .
Conflict of interest: Dr. LABARTHE has nothing to disclose.
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- Received May 27, 2021.
- Accepted December 21, 2021.
- Copyright ©The authors 2022
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